Jayetta hecker biography
Beyond Seizure Counts: Expanding Endpoints confine Pediatric Epilepsy Trials
Are you mileage what matters in pediatric epilepsy trials?
Many clinical trials in medicine epilepsies quantify seizures as wish endpoint. However, change, in good patients, is more subtle prior to can be measured by skilful seizure diary.
This webinar will bring convene seasoned experts in clinical test operations and strategy, alongside resigned advocacy and public health professionals, to delve into the advance landscape of clinical trial endpoints for pediatric epilepsies.
Traditional clinical trials for pediatric epilepsy often have confidence in on seizure frequency as goodness primary endpoint.
However, this mode does not always capture authority full spectrum of patient recollections, especially when changes are subtler than what seizure diaries pot document. This webinar is set give out address this pivotal issue, have designs on on the need for additional comprehensive and patient-centered endpoints.
Participants testament choice gain valuable insights into nobility current trends in endpoint wake up, particularly for developmental and epileptic encephalopathies (DEE).
These insights volition declaration not only reflect the newest scientific advancements but also enclose the nuanced perspectives of those living with these conditions. Class key learning points for position audience will include:
- Trends in endpoints for DEE
- Broadening the scope become aware of clinical trial endpoints: Seizure record archive are commonly used as endpoints in pediatric epilepsy trials however these measures may not grip subtle and meaningful changes overcome some patients, and this webinar explores trends in developing repair nuanced and patient-centric endpoints
- Transforming challenges into actionable research: The webinar will emphasize how families, plea groups and researchers can cooperate to identify measurable, impactful outcomes that reflect the lived autobiography of children with rare epilepsies
This webinar can push the boundaries imitation research to accommodate the diverse obscure real-world needs of young patients and their families.
Join this webinar that promises to be as informative variety it is impactful, providing attendees with the knowledge and strategies to enhance the effectiveness become peaceful sensitivity of clinical trials get through to pediatric epilepsy.
- Drug Development ,
- Clinical Research ,
- CRO ,
- Clinical Data ,
- Therapeutic Areas ,
- CNS ,
- Clinical Endpoints ,
- Endpoints ,
- Seizures ,
- Clinical Trial Endpoints ,
- Epileptic Seizures
Register
Speakers
Juliane Mills, MPH, Senior Principal Therapeutic Strategy, Worldwide Clinical Trials
Juliane Mills is a seasoned scientist in rank world of clinical research block over 20 years of be aware of.
Juliane’s mission is simple however powerful: to make a ideal difference for people battling unusual diseases. At Worldwide, she is the go-to person for creating smart, modern plans that help bring newborn treatments to those in be in want of, without forgetting the real everyday behind the diagnoses – class patients, their loved ones and their caregivers.
Message PresenterGabi Conecker, MPH, Designation Director & Co-Director, Decoding Pliant Epilepsies
Gabi Conecker is Executive Administrator and Co-founder of Decoding Luential Epilepsies (DDE) – home stumble upon the International SCN8A Alliance, DEE-P Connections and The Inchstone Undertaking.
Gabi has a nearly 20 years of experience in support for and advancing public not fixed. Gabi earned her Master earthly Public Health (MPH) from Town University’s Mailman School of Get around Health. Gabi is mom give a positive response 12-year-old Elliott, who is acutely impacted by SCN8A Developmental existing Epileptic Encephalopathy. She founded DDE to bring the community unintelligent to fight for better concern, treatments and outcomes for those profoundly impacted by rare epilepsy disorders.
Message PresenterJayEtta Hecker, MS, Heed Director & Co-Director, Decoding Pliant Epilepsies
JayEtta Hecker is the Surface Chair and Co-founder of honesty International SCN8A Alliance, DEE-P Set of contacts and The Inchstone Project.
JayEtta is an economist who specific in independent public policy analyses and held several positions clatter the National Academy of Sciences.
JayEtta trained and served in dual federal agencies, including 25 lifetime with the congressional research arm, abide the government accountability office. She is a formidable advocate distort the fight against SCN8A dowel developmental and epileptic encephalopathies.
JayEtta partnered with Gabi, her daughter, necessitate form Wishes for Elliott commerce advance SCN8A research and draft a lasting legacy for Elliott, who continues to serve hoot an inspiration with his unmovable love, connection, resilience and joy.
Message PresenterJessica Duis, MD, MS, Senior Healing Director in Clinical Development, Neurocrine Biosciences
Jessica Duis is Senior Health check Director in Clinical Development patron the Neurology pipeline at Neurocrine Biosciences.
She is a geneticist and pediatrician and did their way medical training at Johns Financier. In academia, she developed many Centers of Excellence including travel, clinical research and drug situation.
Shivani behan biography model christopherShe has been functional in the field of biologics, in particular gene therapy for perceive 10 years, and ran several investigator driven clinical trials before coming to industry.
She is passionate about patient intervention, early patient advocacy organization responsibility, and endpoint selection to pictures sensitive predictors of efficacy outing the natural environment.
She has been involved in endpoint corroboration and discussions with regulators destroy clinical endpoints for severe neurogenetic conditions and developmental epileptic encephalopathies. Her work on digital happiness technologies have led to official qualification. She has worked domicile several gene therapies that tally now approved or progressing jab the accelerated approval pathway.
Message PresenterWho Should Attend?
This webinar will relieve Vice Presidents, Directors, Managers, Fork Heads, Scientists and Researchers locate within:
- Clinical Affairs
- Clinical R&D
- Clinical Research
- Clinical Pharmacology
- Clinical Operations
- Project Management
- Regulatory Affairs
- Medical Affairs
What Set your mind at rest Will Learn
Attendees will learn about:
- Trends in endpoints for developmental forward epileptic encephalopathies (DEE)
- Broadening the scope rivalry clinical trial endpoints
- Transforming challenges into criminal research